-
effectivehealthcare.ahrq.gov/health-topics/vascular-diseases?page=3
-
effectivehealthcare.ahrq.gov/health-topics/vascular-diseases?page=4
-
effectivehealthcare.ahrq.gov/health-topics/neurologic-diseases?page=3
-
effectivehealthcare.ahrq.gov/health-topics/neurologic-diseases?page=1
-
effectivehealthcare.ahrq.gov/health-topics/neurologic-diseases?page=5
-
effectivehealthcare.ahrq.gov/health-topics/neurologic-diseases?page=2
-
effectivehealthcare.ahrq.gov/health-topics/neurologic-diseases?page=4
-
effectivehealthcare.ahrq.gov/health-topics/digestive-diseases?page=1
-
effectivehealthcare.ahrq.gov/health-topics/heart-valve-diseases/
-
effectivehealthcare.ahrq.gov/health-topics/animal-diseases-and-your-health
-
effectivehealthcare.ahrq.gov/health-topics/heart-diseases?page=1
-
effectivehealthcare.ahrq.gov/health-topics/heart-diseases?page=2
-
effectivehealthcare.ahrq.gov/health-topics/heart-diseases?page=3
-
effectivehealthcare.ahrq.gov/health-topics/heart-diseases?page=4
-
effectivehealthcare.ahrq.gov/products/rare-diseases-outcomes/executive
July 24, 2014 - Authors with abstracts that were highly rated by a panel of rare disease experts were invited to submit … Quantifying a Rare Disease in Administrative Data: The Example of Calciphylaxis
Nigwekar SU, Solid CA … Quantifying a Rare Disease in Administrative Data: The Example of Calciphylaxis. … Important Role of Translational Science in Rare Disease Innovation, Discovery, and Drug Development … Important Role of Translational Science in Rare Disease Innovation, Discovery, and Drug Development.
-
effectivehealthcare.ahrq.gov/products/rare-diseases-outcomes
July 24, 2014 - Fifth Journal Supplement on Research Methods: Patient-Centered Health Outcomes in Rare Diseases … Fifth Journal Supplement on Research Methods: Patient-Centered Health Outcomes in Rare Diseases
-
effectivehealthcare.ahrq.gov/products/rare-diseases-outcomes/overview
-
effectivehealthcare.ahrq.gov/products/lysosomal-storage-diseases-therapies
October 05, 2011 - Enzyme-Replacement Therapies for Lysosomal Storage Diseases
Timeline
October 04, 2011 … Technical Brief
Archived
Enzyme-Replacement Therapies for Lysosomal Storage Diseases
-
effectivehealthcare.ahrq.gov/sites/default/files/pdf/lysosomal-storage-diseases-therapies_research-protocol.pdf
November 15, 2012 - , lysosomal storage diseases, and rare diseases. … Enzyme reconstitution/replacement
therapy for lysosomal storage diseases. … Current strategies in the management of lysosomal storage diseases. … Update on treatment of lysosomal storage
diseases. Acta Myol 2007 Jul;26(1):87-92. … Diseases with FDA-approved Enzyme Replacement Therapy*
Disease
[estimated
incidence]
Symptoms
-
effectivehealthcare.ahrq.gov/products/lysosomal-storage-diseases-therapies/research-protocol
October 05, 2011 - , lysosomal storage diseases, and rare diseases. … Enzyme reconstitution/replacement therapy for lysosomal storage diseases. … Current strategies in the management of lysosomal storage diseases. … Enzyme replacement for lysosomal diseases. Annu Rev Med 2006;57:283-96. … Diseases with FDA-approved Enzyme Replacement Therapy*
Disease [estimated incidence]
Symptoms
FDA-Approved